News Article


May 15 is International MPS Awareness Day!

Today we:

  • Remember all the children and adults who suffer from MPS and related diseases.
  • Think about the children we have lost.
  • Think about the doctors and scientists who are dedicated to finding a cure for MPS and related diseases.
  • Appreciate each other and are thankful for the strength and support we both give and receive. 

We honor Dr. Emil Kakkis, who developed Aldurazyme®, the enzyme replacement therapy for MPS I, and whose company, Ultragenyx today announced a Phase 1/2 study of UX003 for MPS VII. Read the full press release. Read the Q&A with Dr. Emil Kakkis.

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